FDA Approves First Muscle-Targeted Therapy for SMA

Innovations in Care

We provide programs and services that transform the lives of people affected by neuromuscular disease.

Introducing ISEMBYLD. The first and only FDA-approved treatment for SMA to directly target muscle.

October 6th, 2026
1:30 PM ET
Live, Virtual Webinar

Attendees will learn about the role of muscle in SMA, the importance of directly targeting muscle, how ISEMBYLD works with current SMN2-targeted treatments, its clinical trial results and safety profile, and resources available to support patients throughout their treatment journey.

Register


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