Hope Through Research

At MDA, we take a big picture perspective across the full spectrum of neuromuscular diseases to uncover scientific and medical breakthroughs that accelerate treatments and cures. The power in our research approach is that we can often apply learnings from one disease to progress in others to bring urgently-needed answers to our families.

Clinical Trials & Studies

Clinical trials are key to the search for treatments and cures. Through them, researchers can determine whether experimental new treatments are safe and effective. People who participate in trials help advance science and improve care. 

Search for a Clinical Trial

Amyotrophic Lateral Sclerosis (ALS) 

Charcot-Marie-Tooth Disease (CMT)

Myotonic Muscular Dystrophy 

Congenital Muscular Dystrophy (CMD) 

Duchenne Muscular Dystrophy (DMD) 

Spinal Muscular Atrophy (SMA) 

To see a list of clinical trials in another disease, go to ClinicalTrials.gov, select Search for Clinical Trials, and follow the instructions to narrow down your search results. (ClinicalTrials.gov is a registry of federally and privately supported clinical trials in the United States and around the world.)

Note: This list may include some studies that are not primarily focused on your disease but which make reference to it in some way.

About Clinical Trials

A clinical trial is a test in humans to evaluate biomedical or health-related outcomes, including experimental medications or therapies. Clinical trials are experiments, not treatments, and participation requires careful consideration.

Although it's possible to benefit from participating in a clinical trial, it's also possible that no benefit — or even harm — may occur. Keep your MDA clinic doctor informed about any clinical trial participation.

(Note: MDA has no ability to influence who is chosen to participate in a clinical trial.)

For more about clinical trials in general, see Learning About Clinical Studies.

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