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MDA Engage: Myotonic Dystrophy Symposium

April 28 - 29MDA Engage Logo
Time: 11:00am - 3:00pm Eastern Time
Virtual, online event

There is no cost to members of the MDA community or healthcare providers to attend the event, however registration is required. Members of the biopharma industry interested in sponsoring or attending should contact the MDA Healthcare Partnerships team at For all other questions, please reach out to

Watch Now


4/28: (Times listed are in Eastern Time)

  • Recommended Clinical Practices for Myotonic Dystrophy (11:10am)
    • Dr. Laurie Guttman, Chair, Department of Neurology, Indiana University School of Medicine
  • What is new in Myotonic Research and Clinical Trials (12:15pm)
    • Dr. Jacinda Sampson, Neurogeneticist, Neuromuscular Neurologist & Clinical Professor, Neurology and neurological Sciences, Stanford Health Care
  • Genetic Testing (1:25pm)
    • Tanya Bardakjian, MS, LCGC, University of Pennsylvania
  • Sleep Disorders and Myotonic Dystrophy (2:10pm)
    • Dr. Deanna Diebold, Assistant Professor of Medicine, Division of Pulmonary, Allergy, Critical Care and Sleep Medicine, University of Minnesota


  • The Heart and Myotonic (11:10am)
    • Dr. Matthew Wheeler, Cardiologist, Assistant Professor of Medicine, Stanford University Medical Center
  • The Impact of Respiratory Care (12:10pm)
    • Dr. Michelle Cao, Pulmonologist, Clinical Associate Professor, Neurology & Neurological Sciences Clinical Associate Professor, Psychiatry and Behavioral Sciences, Stanford Center for Sleep Sciences and Medicine
  • MDA Mission Presentation (1:15pm)
    • Nicole Petrouski, Muscular Dystrophy Association
  • GI Issues and Myotonic (1:40pm)
    • Dr. Leila Neshatian, Gastroenterologist, Stanford Medicine

Please check back for updates to the agenda


MDA Thanks our sponsor:

  • Avidity Biosciences