FDA Approves KYGEVVI®, the First and Only Treatment for Thymidine Kinase 2 deficiency (TK2d)

Innovations in Care

We provide programs and services that transform the lives of people affected by neuromuscular disease.

Spinal Muscular Atrophy (SMA)

August 26th, 2025 to August 27th, 2025
August 26th from 3:00pm - 5:00pm EST and Wednesday, August 27th from 3:00pm-5:30pm EST
Live, Virtual Webinar

Join us for a comprehensive, two-day, learning series focused on Spinal Muscular Atrophy (SMA). This series will cover the latest research developments, treatment strategies, and supportive care options for those living with SMA.

Featuring leading neurologists, researchers, and patient advocates, this learning series will provide a comprehensive overview of:

  • What’s Next in Gene Therapy
  • Orthopedic Insights for Everyday Living
  • Managing Respiratory Needs in SMA
  • Pain Management in SMA

Watch On Demand

Whether you're a person living with a neuromuscular disease, a caregiver, family member, or simply interested in learning more, this learning series will offer valuable information and a space to connect with others in the neuromuscular community.

Register now to reserve your spot and be part of the conversation bringing knowledge, resources, and support to the SMA community.

Not available to join live on August 26th and 27th? Register to receive an email when the series is available to view on-demand.

If you have questions about this or other MDA programs, please contact the MDA Resource Center at 1-833-ASK-MDA1 (275-6321) or ResourceCenter@mdausa.org.


Thank you to our supporters:

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