FDA Approves First Muscle-Targeted Therapy for SMA

Innovations in Care

We provide programs and services that transform the lives of people affected by neuromuscular disease.

Sparkle Trial Awareness Webinar

August 13th, 2026
9:00 AM Arizona
Live, Virtual Webinar

The Sparkle Study is a clinical research study testing a possible new (investigational) medicine for children and teenagers with SMA.

Register


Thank you to our supporter:

Argenx