FDA Approves KYGEVVI®, the First and Only Treatment for Thymidine Kinase 2 deficiency (TK2d)

Innovations in Care

We provide programs and services that transform the lives of people affected by neuromuscular disease.

Avidity Biosciences - DMD Functional Data - Topline Results

November 11th, 2025
5:00 PM EST
Live, Virtual Webinar

Please join us for this educational webinar as Avidity Biosciences shares the topline functional data from their EXPLORE44 and EXPLORE44-OLE clinical trials. Their investigational treatment, known as del-zota, is in development for boys and men with Duchenne muscular dystrophy amenable to exon-44 skipping.

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