Innovations in Care
We provide programs and services that transform the lives of people affected by neuromuscular disease.
Research and Care: Next-Generation Genetic Medicines
March 25th, 2026
12:00 PM ET
Live, Virtual Webinar
Join MDA for an informative and in-depth webinar focused on exploring cutting-edge technologies powering the Next-Generation of Genetic Medicines for individuals living with neuromuscular diseases.
While the speakers will discuss applications of these technologies for Duchenne muscular dystrophy (DMD) and limb-girdle muscular dystrophy (LGMD), the tools and approaches discussed are helping to shape therapeutic development across the neuromuscular disease landscape. Whether you are a patient, caregiver, advocate, or community member, this webinar will provide valuable insights into how genetic medicine platforms are advancing, what these breakthroughs could mean for rare neuromuscular conditions broadly, and where the field is heading next.
What We’ll Cover:
- Courtney Young, PhD of MyoGene Bio will present on their preclinical gene editing therapy that targets half of Duchenne muscular dystrophy mutations
- Scot Wolfe, PhD of U Mass Chan Medical School will present on harnessing nature’s tools to repair the genome: a path to therapeutics for Limb-Girdle Muscular Dystrophy.
- Melissa Spencer, PhD of the UCLA Broad Stem Cell Research Center will present the promises and challenges of AAV-based Gene Therapies.
Not available to join live on March 25th? Register to receive an email when the webinar is available to view on-demand.
If you have questions about this webinar or other MDA programs, please contact the MDA Resource Center at 1-833-ASK-MDA1 (275-6321) or ResourceCenter@mdausa.org.
MyoGene Bio
U Mass Chan Medical School
UCLA Broad Stem Cell Research Center
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