Innovations in Care
We provide programs and services that transform the lives of people affected by neuromuscular disease.
Updates in Research and Care: Advances in Gene Therapy- Understanding Options and Decision-Making
December 17th, 2025
4:00pm ET
Live, Virtual Webinar
Join us for an insightful and supportive webinar focused on the latest advances in gene therapy for neuromuscular diseases, including how these therapies work, how they are delivered, and what new treatments could mean for individuals and families.
Whether you're a person living with a neuromuscular disease, caregiver, or advocate, this webinar will offer valuable insights, resources, and support.
What We’ll Cover:
• An overview of the different types of gene therapy being explored for neuromuscular diseases, how they work, how they are delivered, and the challenges researchers are addressing
• How today’s approved treatments are shaping the development of new gene therapies, potentially leading to safer and more effective options
• Updates on gene therapy treatments currently in clinical trials and what they could mean for the future of neuromuscular care
• Live Q&A with the presenter, Dr. Matesanz
Meet Our Presenter:
Susan Matesanz, MD – Children’s Hospital of Philadelphia (CHOP)
Dr. Matesanz is an attending physician and the Medical Director for the Clinical In Vivo Gene Therapy group at the Children’s Hospital of Philadelphia.
Reserve Your Spot Today – It's Free!
Not available to join live on December 17th? Register to receive an email when the webinar is available to view on-demand.
If you have questions about this webinar or other MDA programs, please contact the MDA Resource Center at 1-833-ASK-MDA1 (275-6321) or ResourceCenter@mdausa.org
Children’s Hospital of Philadelphia (CHOP)
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