June is Myasthenia Gravis Awareness Month

Innovations in Care

We provide access to support and programs that empower the lives of people living with neuromuscular diseases.

MDA Engage: Duchenne Muscular Dystrophy (DMD) Symposium

August 8, 2020MDA Engage Logo
Time: 11:00am - 4:30pm ET / 10:00am - 3:30pm CT
Virtual, online event

There is no cost to members of the MDA community or healthcare providers to attend the event, however registration is required. Members of the biopharma industry interested in sponsoring or attending should contact MDAPartners@mdausa.org.

Watch Now


  • Welcome & MDA Mission Spotlight (11:00am ET)
    • Nicole Petrouski, MDA
  • Keynote Presentation: Integrated Care and DMD (11:15am ET)
    • Dr. Brenda Wong, Pediatric Neurologist, UMass Memorial Medical Center
  • Clinical Trials and Research (12:10pm ET)
    • Mattia Quattrocelli, PhD, Research Assistant Professor of Pharmacology, Northwestern University
  • Drug Development Roundtable (12:45pm ET)
  • Genetic Testing (1:40pm ET)
    • Kimberly Zayhowski, MS, CGC, UMass Memorial Medical Center
  • Best Practices in Clinical Care (2:15pm ET)
    • Pulmonary in DMD, Dr. Johnathan Finder, Professor, Pediatric Pulmonology, University of Tennessee Health Science Center
    • Nutrition in DMD, Umme Vahanvaty, MS, RD, CSP, Children’s Hospital Los Angeles
  • Transitioning Care into Adulthood (3:10pm ET)
    • Dr. Leigh Ramos-Platt, Director, Muscular Dystrophy Association Neuromuscular Clinic, Clinical Associate Professor of Pediatrics (Clinician Educator), Keck School of Medicine of USC
  • DME and Assistive Technology (3:45pm ET)
    • Terri Carry, PT, Children’s Hospital Colorado
    • Tim Estilow, OTR/L, Children’s Hospital of Philadelphia (CHOP)


Thank you to our supporters:

  • Fibrogen
  • PTC Therapeutics
  • Sarepta

For questions reach out to: mdaengage@mdausa.org | 1-833-ASK-MDA1 (1-833-275-6321)