FDA Approves First Muscle-Targeted Therapy for SMA

Medical Educational Resource

We're accelerating the delivery of treatments and cures.

A closer look at the first muscle-targeted treatment in SMA

Activity Snapshot

Activity Type: 
Live, Virtual Webinar
Release Date: 
Wednesday, October 7, 2026
Sponsor Information: 

Scholar Rock logo

Activity Overview: 

12:00 PM ET
Scholar Rock introduces ISEMBYLD, the first and only FDA-approved muscle-targeted treatment for SMA. This presentation will explore the persistent unmet need in SMA, the importance of directly targeting muscle, and how ISEMBYLD works alongside SMN2-targeted treatment to improve motor function. Attendees will also learn about the clinical evidence, treatment experience, and resources available through Scholar Rock Supports.