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Agenda Announced for 2024 MDA Clinical & Scientific Conference Featuring Leading Speakers Dedicated to Groundbreaking Research and Clinical Achievements in Neuromuscular Disease

NEW YORK, December 14, 2023 – The Muscular Dystrophy Association today announced the agenda and Chairs for the 2024 MDA Clinical & Scientific Conference being held March 3-6, 2024, in Orlando, Florida. The agenda can be found here.

2024 MDA Clinical & Scientific Conference logo. March 3-6, 2024.
Session agenda and Chairs announced for 2024 MDA Clinical & Scientific Conference.

The 2024 MDA Clinical & Scientific Conference will explore the latest research and clinical achievements for neuromuscular disease in the era of treatments with key sessions led by top industry professionals including:

  • Clinical Considerations – Case Reviews with John Day, MD, PhD and Bakri Elsheikh, MBBS
  • Lab to Life ALS with Rita Sattler, MSc, PhD and Matthew Harms, MD
  • Clinical Approaches to Streamlining Care with Marcia Felker, MD, Elena Caron, MD, Lora Clawson, MSN, CRNP, Gil Wolfe, MD, FAAN, Monika Krzesniak-Swinarska, MD, Meeta Cardon, MD and Amanda Peltier, MD
  • Practical Consideration in Gene Therapy with Holly Paey, PhD and Crystal Proud, MD, John Brandsema, MD, Natalie Goedeker, DNP, CPNP, Julie Parsons, MD and Diedre Devier, PhD
  • Clinical Consideration – Decisions in the Age of Treatment and Life Transitions with Richard Finkel, MD and Jamie Eskuri, MD
  • Lab to Life Ultra-rare, myasthenia gravis,dystrophies, and CMT-- with Alan Beggs, PhD, Linda Kusner, PhD, Katherine Mathews, MD and Michael Shy, MD
  • Disease Mechanism & Therapeutic Strategies with Aaron Beedle, PhD, Jyoti Jaiswal, MSc, PhD, Doug Millay, PhD, Dwi Kemaladewi, PhD, Noah Weisleder, PhD, Vandana Gupta, PhD, MSc and Carlos Moraes, PhD

"The 2024 MDA Conference brings together the world’s leaders in the field of neuromuscular disease research and care. This includes the MDA Care Center Network team members from over 150 locations nationwide. The sessions will cover a broad range of topics, from advancements in clinical care for neuromuscular conditions, to next gen therapeutics like gene editing. The recent FDA approval of the first CRISPR therapy for Sickle Cell Anemia signals major progress for gene editing technology with implications for the neuromuscular community," said Sharon Hesterlee, PhD, Chief Research Officer, Muscular Dystrophy Association. "The conference will feature leading experts from across the continuum of care, including clinicians, affiliated medical professionals, scientific and clinical researchers, and industry partners. Together we’ll explore new techniques for treating and or managing muscular dystrophy, ALS and related neuromuscular diseases."

Members of the neuromuscular disease community who are registered with MDA are welcome to participate in the virtual conference at no-cost or may register here to attend in-person at the patient/caregiver rate until allotted spaces are filled.

For additional information and to register, click here. Early bird registration deadline is December 31, 2023.

The 2024 MDA Clinical & Scientific Conference Social Media Toolkit for registrants, panelists, supporters/sponsors, and advocacy organizations, is available here. MDA will be sharing updates and information on its social media channels using #MDAconference. MDA will be sharing updates and information on its social media channels using #MDAconference.

About the MDA Clinical & Scientific Conference

MDA is the convener of the largest global gathering of the neuromuscular disease community. The four-day international event will bring together renowned researchers, clinicians, academicians, advocates, and industry leaders to explore the latest advances in the field of neuromuscular disease. Last year’s conference included 1,492 in-person and 567 virtual attendees from at least 27 countries, making it the largest worldwide gathering of the neuromuscular disease community.

About Muscular Dystrophy Association

Muscular Dystrophy Association (MDA) is the #1 voluntary health organization in the United States for people living with muscular dystrophy, ALS, and related neuromuscular diseases. For over 70 years, MDA has led the way in accelerating research, advancing care, and advocating for the support of our families. MDA's mission is to empower the people we serve to live longer, more independent lives. To learn more visit and follow MDA on Instagram, Facebook, X, Threads, TikTok, LinkedIn, and YouTube.