FDA Approves First Muscle-Targeted Therapy for SMA

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MDA Case Discussion: Cardiac Care in Neuromuscular Disease

Activity Snapshot

Activity Type: 
On-Demand Webinar
Release Date: 
Wednesday, November 4, 2026
Expiration Date: 
Thursday, October 26, 2028
Sponsor Information: 

This program is supported in part by independent medical education grants to MDA from BridgeBio and PTC Therapeutics, Inc.

Faculty

Linda Cripe, MD
Pediatric Cardiologist, The Heart Center The Neurosciences Center, Neuromuscular Disorders section

Nationwide Children's Hospital

Emily Hayes, MD
Pediatric Cardiologist, The Heart Center Medical Director, Cardiomyopathy Cardiac Director, Neuromuscular Disorders

The Neurosciences Center, Nationwide Children's Hospital

Carol Wittlieb-Weber, MD
Associate Professor of Pediatrics, Perelman School of Medicine at the University of Pennsylvania

Attending Cardiologist, The Children's Hospital of Philadelphia

Activity Overview: 

Cardiologists navigate three patient cases involving cardiomyopathy in pediatric neuromuscular disease. The session aims to improve awareness of available diagnostic tools, therapies, and questions to guide care decisions.
Cases presented by Dr. Carol Witlieb-Weber, Dr. Linda Cripe, and Dr. Emily Hayes.

Learning Objectives: 

• Identify patterns of cardiac involvement in pediatric-onset NMD, including DMD, BMD LGMD, FSHD and FRDA.
• Apply cardiac imaging and ECG findings to support early detection and referral.
• Apply evidence-based approaches to cardiac care, including cardioprotective therapies and arrhythmia risk assessment, as part of a multidisciplinary care team.

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Faculty Disclosures: 

See faculty disclosures here.

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Disclosure of Unlabeled Use and Investigational Product:
This educational activity may include discussion of uses of agents that are investigational and/or unapproved by the FDA. Please refer to the official prescribing information for each product for discussion of approved indications, contraindications, and
warnings.

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