Science + Research

Find the latest science and research updates as well as information to help you understand this ever-evolving field.

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Blog Post

In Case You Missed It…

By MDA Staff | July 8, 2025
Blog Post

Clinical Research Alert: Phase 3 Study of RGX-202 in Boys with DMD

By MDA Staff | June 30, 2025
Plasma donor on Aurora Plasmapheresis System machine.
Blog Post

Simply Stated: MG Therapeutic Landscape

By Sujatha Gurunathan | June 30, 2025
3d illustration showing molecules passing an ion channel in cell membrane
Blog Post

Simply Stated: Updates in Ryanodine Receptor 1-Related Disorders (RYR-1-RD)

By Sujatha Gurunathan | May 29, 2025
Illustration of the neuromuscular junction, where nerves send signals to muscles.
Featured Article

Understanding Congenital Myasthenic Syndrome: Causes and Treatments

By Justine Savage | May 23, 2025
Illustration of a researcher in a white lab coat climbing a ladder shaped like a DNA helix.
Featured Article

Why MDA’s Kickstart Program Is a Game-changer for Gene Therapies

By Amy Bernstein | May 23, 2025
Male doctor giving a speech on a podium at a conference in front of an audience
Blog Post

MDA Conference Grants Support Resources to the Community

By MDA Staff | May 21, 2025
ALS Amyotrophic Lateral Sclerosis - progressive nervous system disease. Amyotrophic lateral sclerosis. Day background design.
Blog Post

Simply Stated: Updates in Amyotrophic Lateral Sclerosis (ALS)

By Sujatha Gurunathan | April 29, 2025
Blog Post

Clinical Research Alert: Observational Study in Female Carriers of SMA and Their Biological Children

By MDA Staff | April 22, 2025
Blog Post

Clinical Research Opportunity: LION-CS101 a Phase 1/2 Study of AB-1003 in Adults with LGMD2I/R9

By MDA Staff | March 31, 2025