Medical Educational Resource
Transition in Patients with Treatable Disorders without Fixed Weakness or Who Experience Slowly Progressive Symptoms around the Age of Transition
This activity has received an educational grant from PTC Therapeutics Inc.
The transition from pediatric to adult care is a challenging time for patients with neuromuscular disease and their families, as well as for providers. Increased use of disease-modifying treatments will likely lead to increased numbers of patients going through the transition process, and providers need to be aware of best practices to ensure this process is beneficial to all stakeholders. Part three of this series will focus on neuromuscular disease patients who have treatable disorders without fixed weakness or who experience slowly progressive symptoms around the age of transition.
- Provide education on how advances in care have impacted, and have the potential to impact, clinical outcomes in patients with neuromuscular disease
- Review available evidence on unmet needs in care transition and provide guidance on best practices for transitioning care in patients with:
- Slowly progressive diseases
- Treatable disorders without fixed weakness
- Provide guidance on multidisciplinary care needs during this transition that are specific to the patient’s disease characteristics
- Identify the benefits of genetic testing prior to transitioning to adult care
- Identify clinical scenarios that can impact the process of transitioning between care settings
This activity has been planned and implemented in accordance with the accreditation requirements and policies of the Accreditation Council for Continuing Medical Education (ACCME) through the joint providership of PeerPoint Medical Education Institute, LLC and Muscular Dystrophy Association. The PeerPoint Medical Education Institute, LLC is accredited by the ACCME to provide continuing medical education for physicians.
The PeerPoint Medical Education Institute, LLC designates this enduring material activity for a maximum of 0.25 AMA PRA Category 1 Credit(s)™. Physicians should claim only the credit commensurate with the extent of their participation in the activity.
Release Date: February 24, 2020
Expiration Date: February 23, 2023
Once you have viewed the program, MDA will share back with you instructions for how to obtain your CME credits. If you have questions on this process, please reach out to email@example.com.
The following presenters, planners, editors, or staff have relevant financial relationships to disclose:
“I, or an immediate family member, have at present or have had within the last 12 months, the following affiliation with one or more organizations that could be perceived as a real or apparent conflict of interest in context to the design, implementation, presentation, evaluation, etc. of CME Activities.”
Ms. Vanessa Battista:
AveXis- Zolgensma; Advisory board participation, Honoraria and travel expenses
Dr. John Brandsema:
Biogen, AveXis, Cytokinetics, PTC, Sarepta, Pfizer, Fibrogen, Alexion; Advisory boards, Speakers' Bureau (Biogen), Contracted research, Consulting fees
All other presenters, planners, editors, or staff reported no relevant relationships with the following statement:
“I, or an immediate family member, do not have at present, or within the last 12 months, nor anticipate having financial interest, arrangement or affiliation with any organizations that could be perceived as a real or apparent conflict of interest in context to the design, implementation, presentation, evaluation, etc. of CME Activities.”
Copyright 2021 Muscular Dystrophy Association. All rights reserved. The Medical Education Program(s) in their entirety (including, but not limited to: webinar(s), speaker deck presentation(s), MDA Monthly Report content and case studies) are owned by Muscular Dystrophy Association and the associated partner(s) and may not be copied, reproduced, or altered in any manner without MDA’s prior written consent except that the User(s) may download, view, or use these program(s) for educational purposes only.
If you wish to alter any of the Medical Education Program(s) presented by the MDA in a form other than what is set out on mda.org, please consult firstname.lastname@example.org.