Hope Through Research

At MDA, we take a big picture perspective across the full spectrum of neuromuscular diseases to uncover scientific and medical breakthroughs that accelerate treatments and cures. The power in our research approach is that we can often apply learnings from one disease to progress in others to bring urgently-needed answers to our families.

Oculopharyngeal Muscular Dystrophy (OPMD)

It is very difficult to develop specific therapies for very rare forms of muscular dystrophy such asĀ oculopharyngeal muscular dystrophy (OPMD). However, potential therapeutics in development for other muscular dystrophies (if successful) also may be effective for these diseases.

Some strategies, such as muscle strengthening drugs or stem cell therapies, may be effective in many muscular dystrophies. MDA also has supported researchers who have worked out the genetic causes of OPMD, and this is a starting point for more specific therapies.

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