A look at causes, symptoms, and care options for neuromuscular diseases, and how we're leading the way to better treatments and cures.
At MDA, we take a big picture perspective across the full spectrum of neuromuscular diseases to uncover scientific and medical breakthroughs that accelerate treatments and cures. The power in our research approach is that we can often apply learnings from one disease to progress in others to bring urgently-needed answers to our families.
The FDA has granted accelerated approval to eteplirsen for the treatment of Duchenne muscular dystrophy! Decades of MDA research and investment have paid off with the first disease-modifying drug available to treat DMD.
We’re taking a big picture approach to accelerating treatments and cures for muscular dystrophy, ALS and related diseases.
A $3 Million NIH Grant follows early MDA support for experimental “dissociative steroid.”
With our collective strength, we will support families in hometowns across America and help everyone with ALS live longer, stronger lives.
“Wild and crazy” Zane Jacobs is determined to live life unlimited despite the challenges of DMD.
Medical centers across the country are now participating in open-label expanded access program (EAP) called ACCESS DMD
Read MDA News to stay up-to-date on issues that matter to the MDA community.
Biomarkers can provide crucial information for researchers conducting clinical trials.
James Ervasti, professor in the department of biochemistry, molecular biology & biophysics at the University of Minnesota in Minneapolis, is working to develop methods of identifying non-invasive biomarkers.
The FDA has approved Taro Pharmaceuticals’ Keveyis 50 mg tablets for primary hyperkalemic and hypokalemic periodic paralysis.
For 42-year-old Warner Smith, treatments and cures for ALS can't come fast enough. Like any doting father, Warner wants to be around for all his young daughter Carlee’s milestone moments. He wants to teach her to drive, see her go to prom and walk her down the aisle at her wedding. Every moment is precious to Warner and his family — all he wants is “a fighting chance.”Watch Video
MDA helps you keep up on research news, health care information and helpful daily living strategies through magazines, print and online publications, educational speakers, seminars, videos and newsletters.
Our trained specialists are here to provide one-on-one support for every part of your journey. Send a message below or call us at 800-572-1717. If you live outside the U.S., we may be able to connect you to muscular dystrophy groups in your area, but MDA services are only available in the U.S.