About Neuromuscular Diseases
A look at causes, symptoms, and care options for neuromuscular diseases, and how we're leading the way to better treatments and cures.
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MDA Grants $3.5 Million in New Research Funding
MDA Grants $3.5 Million in New Research Funding
These worldwide research projects are striving to answer questions, find solutions and make breakthroughs that will lead to treatments and cures.
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Eteplirsen Granted Accelerated Approval
Eteplirsen Granted Accelerated Approval
The FDA has granted accelerated approval to eteplirsen for the treatment of Duchenne muscular dystrophy! Decades of MDA research and investment have paid off with the first disease-modifying drug available to treat DMD.
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MDA Grants $7 Million in New Research Funding
MDA Grants $7 Million in New Research Funding
Following the unprecedented approval of three drugs in six months to treat neuromuscular diseases, we're pushing for more progress with $7 million in new research funding.
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Phase 2 clinical trial will test Vamorolone in boys with DMD
Phase 2 clinical trial will test Vamorolone in boys with DMD
A $3 Million NIH Grant follows early MDA support for experimental “dissociative steroid.”
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Meet Zane
Meet Zane
“Wild and crazy” Zane Jacobs is determined to live life unlimited despite the challenges of DMD.
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Marathon Pharmaceuticals expands DMD patient access to Deflazacort.
Marathon Pharmaceuticals expands DMD patient access to Deflazacort.
Medical centers across the country are now participating in open-label expanded access program (EAP) called ACCESS DMD