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2020 MDA Engage: Gene Replacement Therapy for SMA Webinar

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View the On-demand Webinar

The Muscular Dystrophy Association (MDA) alongside Dr. Crystal Proud and Tanicia Johnson from Children's Hospital of The King's Daughter in Norfolk, VA, are the hosts of this on-demand webinar for Spinal Muscular Atrophy (SMA) families to learn more about gene replacement therapy.  Topics explored during this webinar include an overview of what gene replacement therapy is and how it works, discussion of the approved gene replacement therapy for SMA (Zolgensma), how to navigate the clinical experience, how to manage out of pocket costs as well as learn about the One Gene Program.

This MDA Engage Program is sponsored in part by:

  • AveXis

If you have questions after you watch this on-demand webinar, please reach out to or you may contact our MDA Resource Center at 1-833-ASK-MDA1 (275-6321) or