MDA Applauds Expanded US FDA Approval of ELEVIDYS Gene Therapy for DMD Patients Ages 4 and Above

Innovations in Care

We provide access to support and programs that empower the lives of people living with neuromuscular diseases.

MDA Engage - New Jersey

Saturday, June 3, 2023MDA Engage Logo
9:30am - 4:30pm
Westin Princeton at Forrestal Village
201 Village Blvd, Princeton, NJ 08540



Watch Recordings

MDA is pleased to have Dr. Matthew Harms from Columbia University chairing this Engage Symposium.

Headshot of Matthew Harms, MD
Matthew Harms, MD
Columbia University
Member, MDA Medical Advisory Board

This program is provided at no cost, but registration is required. Breakfast and lunch will be served.


  • Legislative Advocacy: Raising A Collective Voice for Change presented by Mark Fisher, Director of Advocacy Engagement, MDA
    Download Presentation Deck
  • Updates in Research and Clinical Trials for SMA presented by John Brandsema, MD, Children’s Hospital of Philadelphia
    Download Presentation Deck
  • Orthopedic Aspects of Spinal Muscular Atrophy: Evolving Treatments in the Age of Gene Therapy presented by Jason Howard, MD, Nemours Children's Hospital
    Download Presentation Deck

MDA Thanks our sponsors:

  • Apellis
  • Biogen
  • Mitsubishi Tanabe Pharma, America
  • Scholar Rock logo

For sponsorship opportunities or question about these events, please email or call 1-833-ASK-MDA1 (1-833-275-6321) and we’ll be happy to help!