Cristina Csimma, PharmD, MHP
Principal
Clarus Ventures, LLC

Louis M. Kunkel, Ph.D.
Chairman, MDA Scientific Advisory Committee
Associate Director; Professor of Pediatrics
Harvard Medical School/Children's Hospital
Department of Genetics

Elizabeth McNally, M.D., Ph.D.
Professor of Medicine and Human Genetics
Director, Institute for Cardiovascular Research
Director, Cardiovascular Genetics Clinic
University of Chicago Medical Center

Terence Partridge, Ph.D., FmedSci
Center for Genetic Medicine Research
Children’s National Medical Center

John D. Porter, Ph.D.
Program Director, Neuromuscular Disease
Channels, Synapses, and Circuits Cluster
National Institutes of Neurological Disorders and Stroke

Lee Wrubel, M.D.
General Partner
Foundation Medical Partners