Quest Magazine

ABC Television Network Is New Home of MDA Show of Strength Telethon

Western Refining Raises $524,286 to Help Send Kids with Neuromuscular Disease to MDA Summer Camp

Stores across the Southwest exceed 2015 fundraising goal by nearly $100,000.

PHOENIX, July 7, 2015 — More than 260 Western Refining convenience stores throughout the Southwest, including Giant, Mustang, Sun Dial and Howdy’s, raised more than $524,286 during the Muscular Dystrophy Association's summer camp mobile program, surpassing their original 2015 fundraising goal by nearly $100,000, to help support children fighting muscular dystrophy and related life-threatening diseases that limit muscle strength and mobility.

Sarepta Completes NDA for Eteplirsen and FDA Accepts BioMarin NDA for Drisapersen; Two DMD Treatments on Horizon

Background: On Monday, June 29, BioMarin announced  that the FDA has accepted their New Drug Application (NDA) for drisapersen and Sarepta announced that they have completed their NDA submission for eteplirsen. Both "exon-skipping" drugs target exon 51, and may help up to 13% of Duchenne muscular dystrophy patients.

Supreme Court Upholds Nationwide Health Care Law Subsidies in ACA Ruling

Background: On June 25th, 2015 the United States Supreme Court ruled to uphold nationwide health care law subsidies. Under the Affordable Care Act (ACA), states were tasked with setting up their own exchanges where individuals could purchase healthcare. Some states created exchanges, while others opted to use exchanges run by the federal government. The question at issue in the Supreme Court case King v.

Transitions Center Blog - Trusting the Journey

I still can’t believe I ended up in New York.

Isis Pharmaceuticals Reports Data from ISIS-SMN Rx in Children with Type 2 and 3 SMA

Transition to Independence Act (S.1604)

Akashi Therapeutics Reports Data from Phase 1b-2a Study in Boys with Duchenne Muscular Dystrophy

News: Isis Pharmaceuticals Reports Data from Phase 2 Study in Infants with Spinal Muscular Atrophy

It's Myasthenia Gravis Awareness Month 2015

In recognition of June being National Myasthenia Gravis Awareness Month, MDA is examining the disease from several perspectives. This article offers an overview of signs, symptoms, diagnosis and treatments for myasthenia gravis (MG), as well as information on drugs that people with MG should avoid.

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